selected publications
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Journal Article
- Comparative effectiveness of intracerebroventricular, intrathecal, and intranasal routes of AAV9 vector administration for genetic therapy of neurologic disease in murine mucopolysaccharidosis type I. Frontiers in Molecular Neuroscience. 2021
- Lysosomal enzyme can bypass the blood-brain barrier and reach the CNS following intranasal administration. Molecular Genetics and Metabolism. 2012